Gene Therapy: Evolution Of A Revolution

Gene therapy is ushering in a golden age of medicine, as smart scientists and brave patients work together to cure once untreatable diseases, which promises both breakthroughs and challenges for global healthcare.

Gene therapy may be one of the greatest success stories of the 21st century, with many treatments in development and a number of recent approvals. Patients suffering from genetic diseases that were once seen as untreatable, now have hope. Recent successes offer miraculous cures with biblical implications. For example, boys facing paralysis from Duchenne muscular dystrophy are retaining their ability to walk based on preliminary results from an investigational drug being advanced by Pfizer. With over 1000 clinical trials currently underway, we may be witnessing a revolution in the treatment of disease. Gene therapy holds the promise to cure disease by fixing genetic defects at the molecular level.

Director | Tim Finkbiner
Producers | Donna Mitchell, Eva Mancil